'It is nice to have my freedom back and not be in hospital anymore' ...

A young boy, among the first in the UK to receive a revolutionary £1.65 million gene-editing treatment, has returned to the hospital where he was cared for to express his gratitude to the nurse who ...

Always in the best of spirits and with a very strong faith, Jamon Tavio King is facing a battle with a very rare leukemia […] ...

Teenage boy revels in ‘freedom’ after £1.65 million gene-editing treatment - Adam Rehman underwent treatment after previously ...

Virginia Tech researchers have discovered an indication hidden in the brain that may help doctors identify children suffering ...

A clinical trial at Brown University Health to treat chronic low back pain with a one-time, non-surgical injection treatment ...

Caring Cross, a 501(c)(3) non-profit dedicated to improving access to advanced therapies, and Boston Children's Hospital today announced a collaboration to provide a sustainable, affordable pathway ...

NEW YORK – Boston Children's Hospital has granted a worldwide license for an investigational gene therapy for sickle cell disease and beta thalassemia to Caring Cross, the nonprofit announced this ...

Medicaid is doing a novel payment system for the new, promising and expensive sickle cell treatment. It may become a model ...

A rare but severe stem cell transplant complication that often becomes fatal now has its first FDA-approved treatment, a therapy developed by biotechnology company Omeros. The Christmas Eve regulatory ...

Hope Biosciences has linked its stem cell therapy candidate to improved motor function in Parkinson’s disease patients in a phase 2 trial. The single-site study randomized 60 people with early to ...