The American Journal of Managed Care3h
5 Rare Diseases That Now Have Their First FDA-Approved Treatments
Several rare disease patient populations received their first-ever FDA-approved drug since Rare Disease Day last year, ...
BioPharma Dive4h
Praxis hits trial setback; Bristol Myers lays off staff in New Jersey
The brain drug developer is continuing a trial despite a recommendation it be stopped for futility. Elsewhere, Eli Lilly ...
BioSpace6h
6 Rare Diseases That Have New FDA-Approved Treatments
ITF, IntraBio and Orchard are among the companies that have won FDA nods in the past year for Duchenne muscular dystrophy, ...
FiercePharma7h
Arrowhead, Zevra fire up campaigns for Rare Disease Day 2025
Zevra used the awareness day to roll out the “Learn NPC, Read Between the Signs” disease awareness campaign. The biotech won ...
Zevra Therapeutics launches new disease state awareness campaign
Zevra Therapeutics (ZVRA) announced, on Rare Disease Day, the launch of a new disease state awareness campaign, ‘Learn NPC, Read Between the ...
Zevra sells priority review voucher for $150m to support drug launches
Zevra has sold its US Food and Drug Administration (FDA) priority review voucher (PRV) for $150m to an undisclosed party. The ...