The US Food and Drug Administration (FDA) has granted a Priority Review designation to a New Drug Application (NDA) for TransCon ® CNP (navepegritide) for the treatment of children with achondroplasia ...

Physical activity, while not harmful, was not significantly associated with positive outcomes in this study. Physical activity before or during pregnancy was not associated with negative ...

Stem cell therapy, artificial womb technology, and telehealth innovations are reshaping neonatal care and improving outcomes for infants affected by complex conditions, including fetal and neonatal ...

There is significant variability in terms of management practices across Canadian medical centers in terms of red blood cell (RBC) and platelet transfusions in preterm newborns, according to a study ...

A lack of a family history is an impediment to achieving a timely diagnosis in severe hemophilia A and is associated with poorer treatment outcomes, according to a study published in Haemophilia..

It has been suggested that restrictive approaches for platelet transfusions be implemented in relevant adult and pediatric populations, including those with fetal and neonatal alloimmune ...

Complement inhibitor therapy allowed for a larger and more rapid reduction of steroid dosages in patients with generalized myasthenia gravis (gMG) than azathioprine and mycophenolate mofetil, ...

Ibrutinib-based therapy, with or without rituximab, continued to deliver durable responses in patients with chronic lymphocytic leukemia (CLL) after a median follow-up of 114 months, according to ...

An upcoming study aims to assess the pharmacokinetics and pharmacodynamics of migalastat in children with Fabry disease who were under 12 years of age.. Migalastat binds selectively and reversibly to ...

Among term neonates admitted for jaundice, breastfeeding was the only statistically significant risk factor associated with bilirubin levels exceeding the exchange blood transfusion line (EBTL), often ...

Findings from a literature search and meta-analysis have revealed human leukocyte antigen (HLA) susceptibility markers that are predictive of predisposition to antineutrophil cytoplasmic antibody ...

Evaluating HDFN Risk With “Confusing” Blood Group Antibodies, Such as Anti-G, Anti-M ...