Columnist Sherry Toh explains how her doctors demonstrated the correct way to provide a supportive environment for LGBTQ+ ...

Learn what you need to do to have a fun, safe, and stress-free day at an amusement park when you have spinal muscular atrophy.

A trip to England with her friend of 30-plus years prompts columnist Connie Chandler to give thanks for kind friends who ...

Treatment with salanersen slowed neurodegeneration and improved motor function in children with SMA in a Phase 1 trial, ...

Tyler, who has SMA, shares how smart home technology helps support his daily routines, independence, and overall quality of ...

Living with SMA isn't just about survival, says columnist. There's also the emotional weight of preparing for the next crisis ...

Buckle up, it's going to be an incredible ride, columnist Helen Baldwin says in a letter to her 13-year-old self.

Many SMA patients continue to see gains in motor function with long-term Spinraza treatment, a real-world study from ...

Two children experienced improvements in motor milestones after one year of salbutamol treatment. One was able to sit independently and the other to walk unassisted. Before treatment, they could only ...

While more than half (54.3%) of the children were a normal weight at the study’s start (baseline), 26.1% were underweight and 19.6% were overweight. Dietary intake generally remained stable through ...

Lexi and Eric, who both have SMA, grew up together and fell in love — building a life full of humor, heart and figuring it out as they go.