University of California2d
Breathing new life: Working toward an inhalable gene therapy for cystic fibrosis
Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...
Cystic Fibrosis Foundation2d
Cystic Fibrosis Foundation Celebrates New National Volunteer Advocacy Co-Chairs
The Foundation’s National Volunteer Advocacy Committee provides guidance and support to further strengthen and enhance the ...
Cystic fibrosis patients could get new 'once-a-day' pill this year
Cystic fibrosis (CF) patients could be given access to a new drug on the NHS by the end of the year if it is given the green ...
Cystic Fibrosis Foundation4d
Raising a Child With Cystic Fibrosis
After my son, Julius, was diagnosed with cystic fibrosis, I adjusted to his daily treatments and medical routines, and though I feel guilt and sadness seeing him becoming so familiar with his CF ...
NHS hope as new miracle drug greatly reduces some cystic fibrosis symptoms
The genetic condition cystic fibrosis had no treatments on the NHS before 2019 and a Daily Express campaign - now a miracle ...
Shields Gazette on MSN1d
I’m aiming to be the first person with cystic fibrosis to swim all 13 lakes in the Lake District
Adam Ball, from South Shields, has set himself the challenge of swimming all 13 publicly accessible lakes in the Lake ...
UnitedHealth eases rules on renewing some prescription drugs
UnitedHealth Group's pharmacy benefit manager, Optum Rx, said on Wednesday it would ease requirements to get insurance ...
Cystic Fibrosis Clinical Trials and Studies: EMA, PDMA, FDA Approvals, Mechanism of Action, ROA, NDA, IND, and Companies
In March 2025, Vertex Pharmaceuticals Incorporated announced a study is to evaluate the safety, and tolerability and efficacy ...
Vertex Announces Medsafe Consent For TRIKAFTA®To Treat Children With Cystic Fibrosis Ages 2-5 Years
From today, the updated indication for TRIKAFTA is as follows: TRIKAFTA is indicated for the treatment of cystic fibrosis in patients aged 2 years and older who have at least one F508del mutation in ...
Miracle daily pill to help condition suffered by 10,000 people could soon be available on the NHS
A MIRACLE pill that’s been shown to help with many of the symptoms of cystic fibrosis (CF) has been approved for thousands of ...
KATC4d
Cystic Fibrosis Foundation to recognize Acadiana’s top young professionals
The Cystic Fibrosis Foundation will host Acadiana’s Finest, a campaign to raise funds and awareness for cystic fibrosis and recognize the area’s top young professional leaders.
Crime6d
Cystic fibrosis patients could get new 'once-a-day' pill this year
we must never forget these medicines are not a cure, and do not work for everyone. CF continues to make too many lives too tough and too short, and Cystic Fibrosis Trust will not stop until ...