University of California1d
Breathing new life: Working toward an inhalable gene therapy for cystic fibrosis
Although cystic fibrosis is a single gene mutation, there are more than 1,000 different ways the CFTR gene can mutate in ...
NHS hope as new miracle drug greatly reduces some cystic fibrosis symptoms
The genetic condition cystic fibrosis had no treatments on the NHS before 2019 and a Daily Express campaign - now a miracle ...
Cystic Fibrosis Clinical Trials and Studies: EMA, PDMA, FDA Approvals, Mechanism of Action, ROA, NDA, IND, and Companies
In March 2025, Vertex Pharmaceuticals Incorporated announced a study is to evaluate the safety, and tolerability and efficacy ...
Science Daily6d
Newly uncovered mechanism could drive next-gen cystic fibrosis treatments
The Hospital for Sick Children. "Newly uncovered mechanism could drive next-gen cystic fibrosis treatments." ScienceDaily. ScienceDaily, 13 March 2025. <www.sciencedaily.com / releases / 2025 / 03 / ...
UnitedHealth eases rules on renewing some prescription drugs
UnitedHealth Group's pharmacy benefit manager, Optum Rx, said on Wednesday it would ease requirements to get insurance ...
Technology Networks8d
Newly Uncovered Protein Clustering Mechanism Could Drive New Cystic Fibrosis Treatments
Studying how proteins cluster and organize themselves at the cell membrane could pave the way for innovative cystic fibrosis ...
Cystic Fibrosis Foundation1d
Cystic Fibrosis Foundation Celebrates New National Volunteer Advocacy Co-Chairs
The Foundation’s National Volunteer Advocacy Committee provides guidance and support to further strengthen and enhance the ...
Shields Gazette on MSN18h
I’m aiming to be the first person with cystic fibrosis to swim all 13 lakes in the Lake District
Adam Ball, from South Shields, has set himself the challenge of swimming all 13 publicly accessible lakes in the Lake ...
Bishop O'Connell High School's Superdance raises over $260k for cystic fibrosis cure
This year, the Superdance went above and beyond its fundraising goal. “We had an original goal of $150,000. But as of ...
PMLive10d
Vertex’s triple combination cystic fibrosis therapy Alyftrek approved by MHRA
Vertex Pharmaceuticals’ triple combination cystic fibrosis (CF) treatment has been approved by the Medicines and Healthcare ...
Cleveland Daily Banner6d
Lee University to Host 65 Roses 5K to benefit Cystic Fibrosis Research
Roses 5K will be hosted at Lee University as part of the Great Strides event held to raise funds for a cure for cystic ...
Vertex Announces Medsafe Consent For TRIKAFTA®To Treat Children With Cystic Fibrosis Ages 2-5 Years
From today, the updated indication for TRIKAFTA is as follows: TRIKAFTA is indicated for the treatment of cystic fibrosis in patients aged 2 years and older who have at least one F508del mutation in ...